Lentivirus-mediated gene therapy for Fabry disease

Aneal Khan; Dwayne L. Barber; Ju Huang; C. Anthony Rupar; Jack W. Rip; Christiane Auray-Blais; Michel Boutin; Pamela O’Hoski; Kristy Gargulak; William M. McKillop; Graeme Fraser; Syed Wasim; Kaye LeMoine; Shelly Jelinski; Ahsan Chaudhry; Nicole Prokopishyn; Chantal F. Morel; Stephen Couban; Peter R. Duggan; Daniel H. Fowler; Armand Keating; Michael L. West; Ronan Foley; Jeffrey A. Medin

doi:10.1038/s41467-021-21371-5

Lentivirus-mediated gene therapy for Fabry disease

Aneal Khan, Dwayne L. Barber, Ju Huang, C. Anthony Rupar, Jack W. Rip, Christiane Auray-Blais, Michel Boutin, Pamela O’Hoski, Kristy Gargulak, William M. McKillop, Graeme Fraser, Syed Wasim, Kaye LeMoine, Shelly Jelinski, Ahsan Chaudhry, Nicole Prokopishyn, Chantal F. Morel, Stephen Couban, Peter R. Duggan, Daniel H. FowlerArmand Keating, Michael L. West, Ronan Foley, Jeffrey A. Medin

Research output: Contribution to journal › Article › peer-review

81 Citations (Scopus)

Original language	English
Article number	1178
Journal	Nature Communications
Volume	12
Issue number	1
DOIs	https://doi.org/10.1038/s41467-021-21371-5
Publication status	Published - Dec 1 2021
Externally published	Yes

ASJC Scopus Subject Areas

General Physics and Astronomy
General Chemistry
General Biochemistry,Genetics and Molecular Biology

Access to Document

10.1038/s41467-021-21371-5

Cite this

Khan, A., Barber, D. L., Huang, J., Rupar, C. A., Rip, J. W., Auray-Blais, C., Boutin, M., O’Hoski, P., Gargulak, K., McKillop, W. M., Fraser, G., Wasim, S., LeMoine, K., Jelinski, S., Chaudhry, A., Prokopishyn, N., Morel, C. F., Couban, S., Duggan, P. R., ... Medin, J. A. (2021). Lentivirus-mediated gene therapy for Fabry disease. Nature Communications, 12(1), Article 1178. https://doi.org/10.1038/s41467-021-21371-5

Khan, A, Barber, DL, Huang, J, Rupar, CA, Rip, JW, Auray-Blais, C, Boutin, M, O’Hoski, P, Gargulak, K, McKillop, WM, Fraser, G, Wasim, S, LeMoine, K, Jelinski, S, Chaudhry, A, Prokopishyn, N, Morel, CF, Couban, S, Duggan, PR, Fowler, DH, Keating, A, West, ML, Foley, R & Medin, JA 2021, 'Lentivirus-mediated gene therapy for Fabry disease', Nature Communications, vol. 12, no. 1, 1178. https://doi.org/10.1038/s41467-021-21371-5

@article{539ae1dc656d45ee826b396cd33aaf31,

title = "Lentivirus-mediated gene therapy for Fabry disease",

author = "Aneal Khan and Barber, {Dwayne L.} and Ju Huang and Rupar, {C. Anthony} and Rip, {Jack W.} and Christiane Auray-Blais and Michel Boutin and Pamela O{\textquoteright}Hoski and Kristy Gargulak and McKillop, {William M.} and Graeme Fraser and Syed Wasim and Kaye LeMoine and Shelly Jelinski and Ahsan Chaudhry and Nicole Prokopishyn and Morel, {Chantal F.} and Stephen Couban and Duggan, {Peter R.} and Fowler, {Daniel H.} and Armand Keating and West, {Michael L.} and Ronan Foley and Medin, {Jeffrey A.}",

note = "Publisher Copyright: {\textcopyright} 2021, The Author(s).",

year = "2021",

month = dec,

day = "1",

doi = "10.1038/s41467-021-21371-5",

language = "English",

volume = "12",

journal = "Nature Communications",

issn = "2041-1723",

publisher = "Nature Publishing Group",

number = "1",

}

TY - JOUR

T1 - Lentivirus-mediated gene therapy for Fabry disease

AU - Khan, Aneal

AU - Barber, Dwayne L.

AU - Huang, Ju

AU - Rupar, C. Anthony

AU - Rip, Jack W.

AU - Auray-Blais, Christiane

AU - Boutin, Michel

AU - O’Hoski, Pamela

AU - Gargulak, Kristy

AU - McKillop, William M.

AU - Fraser, Graeme

AU - Wasim, Syed

AU - LeMoine, Kaye

AU - Jelinski, Shelly

AU - Chaudhry, Ahsan

AU - Prokopishyn, Nicole

AU - Morel, Chantal F.

AU - Couban, Stephen

AU - Duggan, Peter R.

AU - Fowler, Daniel H.

AU - Keating, Armand

AU - West, Michael L.

AU - Foley, Ronan

AU - Medin, Jeffrey A.

PY - 2021/12/1

Y1 - 2021/12/1

UR - http://www.scopus.com/inward/record.url?scp=85101751131&partnerID=8YFLogxK

UR - http://www.scopus.com/inward/citedby.url?scp=85101751131&partnerID=8YFLogxK

U2 - 10.1038/s41467-021-21371-5

DO - 10.1038/s41467-021-21371-5

M3 - Article

C2 - 33633114

AN - SCOPUS:85101751131

SN - 2041-1723

VL - 12

JO - Nature Communications

JF - Nature Communications

IS - 1

M1 - 1178

ER -

Lentivirus-mediated gene therapy for Fabry disease

ASJC Scopus Subject Areas

Access to Document

Other files and links

Fingerprint

A Canadian success story: world-first to treat Fabry disease with gene therapy

Cite this

Lentivirus-mediated gene therapy for Fabry disease

ASJC Scopus Subject Areas

Access to Document

Other files and links

Fingerprint

Press/Media

A Canadian success story: world-first to treat Fabry disease with gene therapy

Cite this