A National Spinal Muscular Atrophy Registry for Real-World Evidence

Joshua Lounsberry; Saïd M'Dahoma; Emily Butler; Craig Campbell; Alex Mackenzie; Hugh J. McMillan; Louise Simard; Jiri Vajsar; Bernard Brais; Kristine M. Chapman; Nicolas Chrestian; Meghan Crone; Peter Dobrowolski; Susan Dojeiji; James J. Dowling; Nicolas Dupré; Angela Genge; Hernan Gonorazky; Simona Hasal; Aaron Izenberg; Wendy Johnston; Edward Leung; Hanns Lochmüller; Jean K. Mah; Alier Marerro; Rami Massie; Laura McAdam; Anna McCormick; Michel Melanson; Michelle M. Mezei; Cam Tu E. Nguyen; Colleen O'Connell; Erin K. O'Ferrall; Gerald Pfeffer; Cecile Phan; Stephanie Plamondon; Chantal Poulin; Xavier Rodrigue; Kerri L. Schellenberg; Kathy Selby; Jordan Sheriko; Christen Shoesmith; Garth Smith; Monique Taillon; Sean Taylor; Jodi Warman Chardon; Scott Worley; Lawrence Korngut

doi:10.1017/cjn.2020.111

A National Spinal Muscular Atrophy Registry for Real-World Evidence

Joshua Lounsberry, Saïd M'Dahoma, Emily Butler, Craig Campbell, Alex Mackenzie, Hugh J. McMillan, Louise Simard, Jiri Vajsar, Bernard Brais, Kristine M. Chapman, Nicolas Chrestian, Meghan Crone, Peter Dobrowolski, Susan Dojeiji, James J. Dowling, Nicolas Dupré, Angela Genge, Hernan Gonorazky, Simona Hasal, Aaron IzenbergWendy Johnston, Edward Leung, Hanns Lochmüller, Jean K. Mah, Alier Marerro, Rami Massie, Laura McAdam, Anna McCormick, Michel Melanson, Michelle M. Mezei, Cam Tu E. Nguyen, Colleen O'Connell, Erin K. O'Ferrall, Gerald Pfeffer, Cecile Phan, Stephanie Plamondon, Chantal Poulin, Xavier Rodrigue, Kerri L. Schellenberg, Kathy Selby, Jordan Sheriko, Christen Shoesmith, Garth Smith, Monique Taillon, Sean Taylor, Jodi Warman Chardon, Scott Worley, Lawrence Korngut

Veterinary

Research output: Contribution to journal › Article › peer-review

11 Citations (Scopus)

Original language	English
Pages (from-to)	810-815
Number of pages	6
Journal	Canadian Journal of Neurological Sciences
Volume	47
Issue number	6
DOIs	https://doi.org/10.1017/cjn.2020.111
Publication status	Published - Nov 1 2020

ASJC Scopus Subject Areas

Clinical Neurology
Neurology

Keywords

Rare disease
Real-world evidence
Registry
Spinal muscular atrophy

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10.1017/cjn.2020.111

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Lounsberry, J., M'Dahoma, S., Butler, E., Campbell, C., Mackenzie, A., McMillan, H. J., Simard, L., Vajsar, J., Brais, B., Chapman, K. M., Chrestian, N., Crone, M., Dobrowolski, P., Dojeiji, S., Dowling, J. J., Dupré, N., Genge, A., Gonorazky, H., Hasal, S., ... Korngut, L. (2020). A National Spinal Muscular Atrophy Registry for Real-World Evidence. Canadian Journal of Neurological Sciences, 47(6), 810-815. https://doi.org/10.1017/cjn.2020.111

Lounsberry, J, M'Dahoma, S, Butler, E, Campbell, C, Mackenzie, A, McMillan, HJ, Simard, L, Vajsar, J, Brais, B, Chapman, KM, Chrestian, N, Crone, M, Dobrowolski, P, Dojeiji, S, Dowling, JJ, Dupré, N, Genge, A, Gonorazky, H, Hasal, S, Izenberg, A, Johnston, W, Leung, E, Lochmüller, H, Mah, JK, Marerro, A, Massie, R, McAdam, L, McCormick, A, Melanson, M, Mezei, MM, Nguyen, CTE, O'Connell, C, O'Ferrall, EK, Pfeffer, G, Phan, C, Plamondon, S, Poulin, C, Rodrigue, X, Schellenberg, KL, Selby, K, Sheriko, J, Shoesmith, C, Smith, G, Taillon, M, Taylor, S, Warman Chardon, J, Worley, S & Korngut, L 2020, 'A National Spinal Muscular Atrophy Registry for Real-World Evidence', Canadian Journal of Neurological Sciences, vol. 47, no. 6, pp. 810-815. https://doi.org/10.1017/cjn.2020.111

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title = "A National Spinal Muscular Atrophy Registry for Real-World Evidence",

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author = "Joshua Lounsberry and Sa{\"i}d M'Dahoma and Emily Butler and Craig Campbell and Alex Mackenzie and McMillan, {Hugh J.} and Louise Simard and Jiri Vajsar and Bernard Brais and Chapman, {Kristine M.} and Nicolas Chrestian and Meghan Crone and Peter Dobrowolski and Susan Dojeiji and Dowling, {James J.} and Nicolas Dupr{\'e} and Angela Genge and Hernan Gonorazky and Simona Hasal and Aaron Izenberg and Wendy Johnston and Edward Leung and Hanns Lochm{\"u}ller and Mah, {Jean K.} and Alier Marerro and Rami Massie and Laura McAdam and Anna McCormick and Michel Melanson and Mezei, {Michelle M.} and Nguyen, {Cam Tu E.} and Colleen O'Connell and O'Ferrall, {Erin K.} and Gerald Pfeffer and Cecile Phan and Stephanie Plamondon and Chantal Poulin and Xavier Rodrigue and Schellenberg, {Kerri L.} and Kathy Selby and Jordan Sheriko and Christen Shoesmith and Garth Smith and Monique Taillon and Sean Taylor and {Warman Chardon}, Jodi and Scott Worley and Lawrence Korngut",

note = "Publisher Copyright: Copyright {\textcopyright} The Author(s), 2020. Published by Cambridge University Press on behalf of The Canadian Journal of Neurological Sciences Inc..",

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AU - Lounsberry, Joshua

AU - M'Dahoma, Saïd

AU - Butler, Emily

AU - Campbell, Craig

AU - Mackenzie, Alex

AU - McMillan, Hugh J.

AU - Simard, Louise

AU - Vajsar, Jiri

AU - Brais, Bernard

AU - Chapman, Kristine M.

AU - Chrestian, Nicolas

AU - Crone, Meghan

AU - Dobrowolski, Peter

AU - Dojeiji, Susan

AU - Dowling, James J.

AU - Dupré, Nicolas

AU - Genge, Angela

AU - Gonorazky, Hernan

AU - Hasal, Simona

AU - Izenberg, Aaron

AU - Johnston, Wendy

AU - Leung, Edward

AU - Lochmüller, Hanns

AU - Mah, Jean K.

AU - Marerro, Alier

AU - Massie, Rami

AU - McAdam, Laura

AU - McCormick, Anna

AU - Melanson, Michel

AU - Mezei, Michelle M.

AU - Nguyen, Cam Tu E.

AU - O'Connell, Colleen

AU - O'Ferrall, Erin K.

AU - Pfeffer, Gerald

AU - Phan, Cecile

AU - Plamondon, Stephanie

AU - Poulin, Chantal

AU - Rodrigue, Xavier

AU - Schellenberg, Kerri L.

AU - Selby, Kathy

AU - Sheriko, Jordan

AU - Shoesmith, Christen

AU - Smith, Garth

AU - Taillon, Monique

AU - Taylor, Sean

AU - Warman Chardon, Jodi

AU - Worley, Scott

AU - Korngut, Lawrence

PY - 2020/11/1

Y1 - 2020/11/1

KW - Rare disease

KW - Real-world evidence

KW - Registry

KW - Spinal muscular atrophy

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JO - Canadian Journal of Neurological Sciences

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A National Spinal Muscular Atrophy Registry for Real-World Evidence

ASJC Scopus Subject Areas

Keywords

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